Xenpozyme
I-Olipudase alfa-rpcp injection isetyenziselwa ukwelapha izimpawu ezingezona ze-nervous system ezingaphansi kwesifo se-acid sphingomyelinase deficiency (ASMD). I-ASMD yisifo sokuzalwa esithinta amalungu omzimba amaningi (isib. isibindi, amaphaphu, ispleen, igazi, isisu) futhi singaba sibi ngokuhamba kwesikhathi. Lolu dokotela kufanele lunikezwe kuphela ngudokotela wakho noma ngaphansi kokunakekelwa kwakhe okuqondile. Lo mkhiqizo uyatholakala ngezindlela zokwelapha ezilandelayo:
Ekucatshangeni kokusebenzisa imithi, izingozi zokuthatha imithi kufanele ziqhathaniswe nezinzuzo ezizoletha. Lo ngumqulu ozothatha wena nodokotela wakho. Kule mithi, okulandelayo kufanele kucabangelwe: Tshela udokotela wakho uma uke waba nanoma yiluphi uhlobo oluqakathekile noma oluhambisana nokwaleka kule mithi noma kwezinye izidakamizwa. Tshela futhi ochwepheshe bakho bezempilo uma unezinye izinhlobo zokwaleka, njengokudla, izibenge, izigcini, noma izilwane. Ngomkhiqizo ongenayo iresiphi, funda ilebula noma izithako zephakheji ngokucophelela. Izifundo ezifanele ezenziwe kuze kube yimanje azibonisi izinkinga ezikhethekile zabantwana ezingalinda ukusetshenziswa kokubeka i-olipudase alfa-rpcp kubantwana. Ukuphepha nokuphumelela kuye kwaqiniswa. Azikho izifundo ezifanele eziphathelene nobudlelwano bobudala nemiphumela yokubeka i-olipudase alfa-rpcp ezenziwe kubantu abadala. Ayikho izifundo ezifanele kwabesifazane zokunquma ingozi yengane uma usebenzisa le mithi ngesikhathi sokuncelisa. Linganisa izinzuzo ezingaba khona nezingozi ezingaba khona ngaphambi kokuthatha le mithi ngesikhathi sokuncelisa. Nakuba ezinye izidakamizwa kufanele zingasetshenziswa ndawonye nhlobo, kwezinye izimo izidakamizwa ezimbili ezahlukene zingasetshenziswa ndawonye ngisho noma kungenzeka ukuthi kube khona ukusebenzisana. Kulezi zimo, udokotela wakho angafuna ukushintsha umthamo, noma ezinye izinyathelo zokuphepha kungadingeka. Tshela ochwepheshe bakho bezempilo uma uthatha noma iyiphi enye imithi yesikripthi noma engekho esikripthi (over-the-counter [OTC]). Ezinye izidakamizwa akufanele zisetshenziswe ngesikhathi noma eduze kwesikhathi sokudla ukudla noma ukudla izinhlobo ezithile zokudla njengoba kungenzeka kube khona ukusebenzisana. Ukusebenzisa utshwala noma utshaba ngezinye izidakamizwa kungabangela ukusebenzisana. Xoxa nochwepheshe bakho bezempilo ngokusetshenziswa kwemithi yakho ngokudla, utshwala, noma utshaba.
Udokotela noma omunye ochwepheshe bezempilo oqeqeshwe ngokucophelela uzokunika wena noma ingane yakho le miyekezo esikhungweni sezempilo. Inikezwa ngenhlanzi ebekwe kwenye yezinsimbi zakho. Le miyekezo kufanele inikezwe kancane, ngakho-ke i-needle kufanele ihlale ibekwe okungenani imizuzu engama-20. Ngokuvamile inikezwa njalo ngemva kwamasonto ama-2. Ungase futhi uthole imithi (eg, imithi yokwelapha ukwanda, imithi yokwelapha ubushushu, ama-steroids) ukusiza ukuvimbela imiphumela engathandeki ngesikhathi sokuhlungwa. Shaya udokotela wakho noma umthengisi wemithi ukuze uthole imiyalo.
Umshwana wokuzihlangula: I-August iyinkundla yolwazi lwezempilo futhi izimpendulo zayo azihlanganisi iseluleko sezokwelapha. Njalo thintana nochwepheshe bezokwelapha onelayisensi eduze nawe ngaphambi kokwenza noma yiluphi ushintsho.